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publicationDate 2022-04-05-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-11293025-B2
titleOfInvention Compositions and methods for modulating Ataxin 3 expression
abstract Disclosed are methods for modulating splicing of Ataxin 3 mRNA in an animal with modified oligonucleotides. Such compounds and methods are useful to treat, prevent, or ameliorate spinocerebellar ataxia type 3 (SCA3) in an individual in need thereof.
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Total number of triples: 455.