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filingDate 2011-02-03-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_4fa85491fed4e989141f6c26375fac4a
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publicationDate 2011-08-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2011097388-A1
titleOfInvention Selective inhibition of polyglutamine protein expression
abstract The present invention relates to the selective inhibition of protein expression of CAG repeat-related disease proteins such as Huntingtin Disease Protein and Ataxin-3 using double- stranded RNAs and nucleic acid analogs. Chemically-modified RNAs having at least one mismatch as compared to the target CAG repeat sequence are specifically contemplated.
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