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filingDate 2013-05-16-04:00^^<http://www.w3.org/2001/XMLSchema#date>
grantDate 2018-08-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_530f4bc7c3e5c792b567eb3fe55abf2a
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publicationDate 2018-08-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-10059941-B2
titleOfInvention Compositions and methods for modulating SMN gene family expression
abstract Aspects of the invention provide single stranded oligonucleotides for activating or enhancing expression of SMN1 or SMN2. Further aspects provide compositions and kits comprising single stranded oligonucleotides for activating or enhancing expression of SMN1 or SMN2 that comprises exon 7. Methods for modulating expression of SMN1 or SMN2 using the single stranded oligonucleotides are also provided. Further aspects of the invention provide methods for selecting a candidate oligonucleotide for activating or enhancing expression of SMN1 or SMN2.
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Total number of triples: 1167.