Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_42cb9958a3077d03a9d8826e336076b7 http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_2a7ebd2ce5ef7e691bd44c48a88a2bfc http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_5a0c01dfdfe4a6d76d9d74a785bdef3b |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3231 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-343 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3521 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3533 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-315 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-321 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-322 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3517 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C07H21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-1131 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-1132 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-00 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7125 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7115 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-712 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C07H21-00 |
filingDate |
2013-05-16-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
grantDate |
2018-08-28-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_530f4bc7c3e5c792b567eb3fe55abf2a http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_da64a7a375ff9148b61a4525eb4550c7 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_c950d70bf908acb73540b6fdec670e5a http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f338d429f27ed405950fe539982bfe8c |
publicationDate |
2018-08-28-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
US-10059941-B2 |
titleOfInvention |
Compositions and methods for modulating SMN gene family expression |
abstract |
Aspects of the invention provide single stranded oligonucleotides for activating or enhancing expression of SMN1 or SMN2. Further aspects provide compositions and kits comprising single stranded oligonucleotides for activating or enhancing expression of SMN1 or SMN2 that comprises exon 7. Methods for modulating expression of SMN1 or SMN2 using the single stranded oligonucleotides are also provided. Further aspects of the invention provide methods for selecting a candidate oligonucleotide for activating or enhancing expression of SMN1 or SMN2. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2021030766-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11299737-B1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11596646-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10837014-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11185079-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11142768-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2023034983-A3 |
priorityDate |
2012-05-16-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |