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publicationDate 2023-01-03-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-11542501-B2
titleOfInvention Antisense oligonucleotides targeting ATXN3
abstract The present invention relates to antisense LNA oligonucleotides (oligomers) complementary to ATXN3 pre-mRNA sequences, which are capable of inhibiting the expression of ATXN3 protein. Inhibition of ATXN3 expression is beneficial for the treatment of spinocerebellar ataxia.
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