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publicationDate 2013-09-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2013138353-A2
titleOfInvention Compositions and methods for modulation of atxn3 expression
abstract Disclosed are oligonucleotides which target and hybridize to nucleic acid molecules encoding ATXN3, leading to reduced expression of ATXN3, Reduction in the expression of aberrant ATXN3 is beneficial for the treatment of certain medical disorders, such as spinocerebellar ataxia 3.
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Total number of triples: 564.