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filingDate 2021-05-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-11-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2021230286-A1
titleOfInvention Compound, method and pharmaceutical composition for regulating expression of ataxin 3
abstract A modified oligonucleotide that has an activity of inhibiting the expression of Ataxin 3 and has any of the following nucleic acid base sequences or a nucleic acid base sequence having 17 consecutive bases contained in the nucleic acid base sequences. 1) TCGGGTAAGTAGATTTTC (SEQ ID NO. 239), 2) GAAGTATCTGTAGGCCTA (SEQ ID NO. 240), 3) GGACTGTATAGGAGATTA (SEQ ID NO. 241), 4) GGTTATAGGATGCAGGTA (SEQ ID NO.242), 5) AGGTTATAGGATGCAGGT (SEQ ID NO.243), 6) GAAGCTAAGTAGGTGACT (SEQ ID NO. 244), 7) TGAAGCTAAGTAGGTGAC (SEQ ID NO. 245), 8) CCTAGTCACTTTGATAGA (SEQ ID NO. 246), 9) GGAACATCTTGAGTAGGT (SEQ ID NO. 247), 10) GGTGTTCAGGGTAGATGT (SEQ ID NO. 248), 11) GGATACTCTGCCCTGTTC (SEQ ID NO. 249), 12) GGTGTCAAACGTGTGGTT (SEQ ID NO. 250), 13) CCGTGTGCTAGTATTTGT (SEQ ID NO. 251), 14) TAGTAGAGTTTTGCTTGG (SEQ ID NO.252), 15) GATGTAGTAGAGTTTTGC (SEQ ID NO. 253), 16) TGATGTAGTAGAGTTTTG (SEQ ID NO. 254), 17) CTGATGTAGTAGAGTTTT (SEQ ID NO. 255), 19)GCAAGTTGGTTTGTGGTA (SEQ ID NO. 256), 20) TCTAGGCAATTGTGGTGG (SEQ ID NO. 257), 21) GTAACTCTGCACTTCCCA (SEQ ID NO. 258), 22) GTCATCCCTATGTCTTAT (SEQ ID NO. 259), 23) GTCATATGGTCAGGGTAT (SEQ ID NO. 260), 24) TGTCATATGGTCAGGGTA (SEQ ID NO. 261), 25) ATGTCATATGGTCAGGGT (SEQ ID NO. 262) and 26) TATGTCATATGGTCAGGG (SEQ ID NO. 263).
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