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publicationDate 2023-01-03-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-11542506-B2
titleOfInvention Compositions and methods of treating amyotrophic lateral sclerosis (ALS)
abstract The present invention relates to small interfering RNA (siRNA) molecules against the SOD1 gene, adeno-associated viral (AAV) vectors encoding siRNA molecules and methods for treating amyotrophic lateral sclerosis (ALS) using the siRNA molecules and AAV vectors.
priorityDate 2014-11-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB2ZDY1
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID410862584
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02075
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID519904
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02053
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02058
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02040
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID33351
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ97BJ8
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID406367
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00361
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Total number of triples: 1946.