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titleOfInvention Materials and methods for treatment of amyotrophic lateral sclerosis and/or frontal temporal lobular degeneration
abstract The present application provides materials and methods for treating a patient with Amyotrophic Lateral Sclerosis (ALS) and/or Frontaltemporal Lobular Degeneration (FTLD), both ex vivo and in vivo . In addition, the present application provides materials and methods for editing to modulate the expression, function or activity of the C9ORF72 gene in a cell by genome editing.
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7012
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4914
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID66586615
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID12310447
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395408
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226396230
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395503
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3121
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395486
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395485
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226585001
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6274
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226394363
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135444779
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226414019
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID994
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135398679
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID54243814
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226406087
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID18604151
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID44228659
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID21989764
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395888
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6175
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID9877416
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6029
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226402238
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5743
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226414690
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID71593
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226530916
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID54676860
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID773
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226424360
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399383
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID232
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226424302
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399382
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID857
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226424301
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395085
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID15793
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID102175
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226513796
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57478391
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135398658
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226398727
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5258
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57205233
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID24749
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226414875
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6306
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399605
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID8378
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226496471
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135509071
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226496470
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395976
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6694
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID65075
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135398641
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID12917729
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5070
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399239
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4775
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID21872864
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226414273
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID67955
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226413813
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399811
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID791
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID2118
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Total number of triples: 424.