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filingDate 2018-11-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-02-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-10905707-B2
titleOfInvention Compositions and methods for the treatment of expanded repeat-associated disorders
abstract Translation modulating agents that modulate expression of one or more translation start sites for expanded repeat (e.g., DPR) protein synthesis are provided. Compositions and methods for treating translation start sites for expanded repeat (e.g., DPR) protein synthesis-associated disorders are also provided.
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Total number of triples: 558.