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publicationDate 2022-03-16-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-3967758-A1
titleOfInvention Materials and methods for treatment of alpha-1 antitrypsin deficiency
abstract The present application provides materials and methods for treating a patient with alpha-1 antitrypsin deficiency (AATD) both ex vivo and in vivo. In addition, the present application provides materials and methods for editing the SERPINA1 gene in a cell by genome editing.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID32322
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5FKZ1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5NQ29
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP49183
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP41927
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8P126
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13159
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100534514
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9TQY7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24825
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24577
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID109245983
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA8F7B3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID395833
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID10245
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2942904
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID58062900
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6437371
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8NVG5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID531945
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3647081
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID65040
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419574686
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID23778904
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID116499
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID422601260
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5QWC7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID33461
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID553551
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID415742002
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID397435
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419521634
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID652
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30560
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID487
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ4L800
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1261065
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9INJ1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68269
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3121
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68270
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1261299
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9JFB7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3P292
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1261396
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ927U9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ03221
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB5ZCA9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1261578
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO96720
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2897887
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID464393
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A5G4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8VVL0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9K6F0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID112442685
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID131813
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ3BM98
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID10207015
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5WYR3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1209982
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ921I1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ4QN19
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO57203
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15113
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID9615654
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID10376
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68506
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5X7B5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68507
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68508
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP81423
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID1314
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP60574
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID457834276
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68564
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID415824726
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID319583
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID420332
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3981
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57203972
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID102139456
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID10174453
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419490851
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419517187
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8628862
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9EQY0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF5HB62
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9RSY5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01316
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP06478
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID421182355
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID728378
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP81025
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8XFQ8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01317
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01319
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID415728323
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01320
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID927421
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0K7G9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID60923442
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01321

Total number of triples: 1043.