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filingDate 2006-10-27-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_84699776c8d588f1008b1bdd5a6a936d
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publicationDate 2011-05-25-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-2325315-A1
titleOfInvention Compositions and methods for inhibiting expression of huntingtin gene
abstract The invention relates to a double-stranded ribonucleic acid (dsRNA) for inhibiting the expression of the Huntingtin gene (HD gene), comprising an antisense strand having a nucleotide sequence which is less than 25 nucleotides in length and which is substantially complementary to at least a part of the HD gene. The invention also relates to a pharmaceutical composition comprising the dsRNA together with a pharmaceutically acceptable carrier; methods for treating diseases caused by the expression of the HD gene, or a mutant form thereof, using the pharmaceutical composition; and methods for inhibiting the expression of the huntingtin gene in a cell.
priorityDate 2005-10-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 584.