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publicationDate 2013-05-30-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2013078316-A1
titleOfInvention Recombinant adeno-associated virus delivery of alpha-sarcoglycan polynucleotides
abstract The present invention relates to recombinant adeno-associated virus (rAAV) delivery of an alpha-sarcoglycan gene. The invention provides rAAV products and methods of using the rAAV in the treatment of limb girdle muscular dystrophies such as LGMD2D.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID280765
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ28635
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID186816
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9GLG7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB3EWE0
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB3EWD8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID317731
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID10585
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB3EWD4
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48675
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Total number of triples: 596.