abstract |
The present invention relates to adeno-associated virus (AAV) serotype AAV-Rh74 and related AAV vectors, and AAV-Rh74 and related AAV vector mediated gene transfer methods and uses. In particular, AAV-Rh74 and related AAV vectors may be used to express polynucleotides for cells, tissues, or organs for expression (transcription) of genes encoding therapeutic proteins and peptides, and polynucleotides that act as, or are transcribed, . |