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publicationDate 2022-05-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber US-11332760-B2
titleOfInvention Compositions and methods for genomic editing by insertion of donor polynucleotides
abstract The present disclosure provides donor polynucleotides, genome editing systems, methods, pharmaceutical compositions, and kits which correct or induce a mutation that causes Glycogen Storage Disease 1a in a genomic DNA (gDNA) molecule in a cell. In some embodiments the present disclosure provides donor polynucleotides comprising two strands capable of correcting a mutation that causes Glycogen Storage Disease 1a.
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226774021
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID447799215
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226773771
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419474481
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57163429
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226774023
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID1715220
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57163243
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226774022
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID828213
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID637517
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396725
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID615844
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID413565284
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP42740
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID89486891
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP42739
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID14387
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57161944
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID64362
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID25634
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID94312
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226483059
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP69097
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226483058
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04353
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100799042
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226773102
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID240672295
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID33629
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62975
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID66973675
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID156464086
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID23391556
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA8GGN3
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226771766
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID421310364
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419514412
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID21839149
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226771765
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID421310359
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419588331
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135398641
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226771925
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID115234
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID94196
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO94739
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID94190
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226772212
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57257928
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID422121780
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00722
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID33836
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID11886
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO18998
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http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID38300
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419541188
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO96102
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3674
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID140214

Total number of triples: 1643.