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filingDate 2014-11-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationNumber US-9528109-B2
titleOfInvention Methods and means for efficient skipping of exon 45 in duchenne muscular dystrophy pre-mRNA
abstract The invention relates to a method for inducing or promoting skipping of exon 45 of DMD pre-mRNA in a Duchenne Muscular Dystrophy patient, preferably in an isolated (muscle) cell, the method comprising providing an isolated muscle cell with a molecule that binds to a continuous stretch of at least 21 nucleotides within the exon. The invention further relates to such molecule used in the method.
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID17874299
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226417276
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226446129
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID17958707
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID171548
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID18764630
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID8442
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226513633
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226509587
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226509588
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID23188328
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399873

Total number of triples: 283.