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publicationDate 2021-10-21-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2021209521-A1
titleOfInvention Vectors for the treatment of acid ceramidase deficiency
abstract The present invention relates to a vector comprising an ASAH1 open reading frame, for use in the treatment of acid ceramidase deficiency.
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