| Predicate |
Object |
| assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_2daab86f05ec8869f08618d8e586e60e
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_15d42f684941d5b0617ca7764ebdff07
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_bca398c5eb8342cae9b3d774cf8b2fb3 |
| classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2750-14143
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12Y302-01045 |
| classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K38-47
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P3-00
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-0075
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12Y302-01045
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-86 |
| classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-86 |
| filingDate |
2008-06-02-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
| inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f8848949ad3e3da5640f52e831f86a32
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_5a38ae346b6704b1d925548fb4ecaf85 |
| publicationDate |
2008-12-18-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
| publicationNumber |
WO-2008154198-A1 |
| titleOfInvention |
Gene therapy for lysosomal storage diseases |
| abstract |
This disclosure provides methods and compositions for treating lysosomal storage diseases in a subject. In one aspect of the invention, a transgene product is delivered to a subject by administering a recombinant neurotrophic viral vector containing the transgene to the brain. The viral vector delivers the transgene to a region of the brain which is susceptible to infection by the virus and which expresses the encoded recombinant viral gene product. Also provided are compositions for delivery of a transgene product to a subject by administering a recombinant neurotrophic viral vector containing the transgene to the subject's brain. The transgene product may be any that is deficient in a lysosomal storage disease. |
| isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11407996-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3794131-A4
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11103596-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11542525-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10905776-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-8242086-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11590210-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/IL-259964-B
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10287579-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11578340-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10689420-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10829783-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10731178-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-9951328-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11020443-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3952924-A4
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2017106313-A1
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2021209521-A1 |
| priorityDate |
2007-06-06-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
| type |
http://data.epo.org/linked-data/def/patent/Publication |