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publicationNumber WO-2019232208-A1
titleOfInvention Cationic lipids comprising a steroidal moiety
abstract Disclosed are cationic lipids which are compounds of Formula I. Cationic lipids provided herein can be useful for delivery and expression of mRNA and encoded protein, e.g., as a component of liposomal delivery vehicle, and accordingly can be useful for treating various diseases, disorders and conditions, such as those associated with deficiency of one or more proteins.
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Total number of triples: 509.