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publicationDate 2015-09-24-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2015143418-A2
titleOfInvention Gene therapy for retinitis pigmentosa
abstract Provided herein are methods for treating retinitis pigmentosa using an AAV particles encoding miR-708. In one aspect, viral particles are administered to the eye of a human subject; for example, by subretinal injection. Viral particles comprising AAV5 capsids or mutants thereof are contemplated.
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