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filingDate 2011-03-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_46179faea096dcf79ccfd241d8b6833e
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publicationDate 2011-09-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2011113889-A1
titleOfInvention Modified u7 snrnas for treatment of neuromuscular diseases
abstract The present invention relates to a method to improve the activity of engineered U7 snRNAs used in the context of RNA-based therapeutics; particularly in exon skipping, exon inclusion, and mRNA eradication strategies. The resulting modified U7 snRNAs are useful for treating neuromuscular diseases, in particular Duchenne neuromuscular dystrophy, myotonic dystrophy DM1 and spinal muscular atrophy.
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA1RV79
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01651
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01308
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A9B3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0B879
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59800
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59906
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A9B5
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419534993
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID8097
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID794339
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3873434
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP81881
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID407972
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP31001
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13190
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO13339
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8LKW0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO77448
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID281492
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2542002
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP57384
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1465
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6VIW4
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4WIW2
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO59494
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID497091
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP29272
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9V1P1
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA2BLC6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID64301
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ47526
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9A6M9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP36375
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9NDE7
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP29335
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100240709
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP16858
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP94915
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP41522
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DV59
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100009074
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4FZL2
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0QWW2
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID856609
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID543675
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB18
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3MQN0
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP71276
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396218
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Total number of triples: 405.