Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_8268e39ce70ff2ad19742e2a21d5a90c |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2510-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-14 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K48-00 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C07H21-04 |
classificationIPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7105 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C07H21-02 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C07H21-04 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-113 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-63 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N5-10 |
filingDate |
2004-09-13-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_a9b770194560089fab2e2b6d6b3e82c6 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_135c2c3b9bd8007e038386eff67af44f |
publicationDate |
2009-05-07-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
US-2009118206-A1 |
titleOfInvention |
Rna interference for the treatment of gain-of-function disorders |
abstract |
The present invention relates to the discovery of an effective treatment for a variety of gain-of-function diseases, in particular, Huntington's disease (HD). The present invention utilizes RNA Interference technology (RNAi) against polymorphic regions in the genes encoding various gain-of-function mutant proteins resulting in an effective treatment for the gain-of-function disease. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2010151470-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10584337-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-9914924-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10570395-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2007259827-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11193129-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11198873-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2017201258-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11752181-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-2010267810-A1 |
priorityDate |
2003-09-12-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |