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titleOfInvention Methods for treating progeroid laminopathies using oligonucleotide analogues targeting human LMNA
abstract Provided are methods of treatment in subjects having progeroid diseases and related conditions which rely upon LMNA-targeted antisense oligonucleotides for reducing expression of one or more aberrantly spliced LMNA mRNA isoforms that encode progerin.
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Total number of triples: 740.