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filingDate 2005-08-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_04d08c5f468ed447e46056639eaa37a5
publicationDate 2009-01-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber EP-2014309-A1
titleOfInvention Lentiviral vector for exon skipping in a gene encoding a dispensable-domain protein
abstract The invention relates to a lentiviral vector comprising: a modified snRNA sequence of type U7; the native U7 promoter; at least one antisense sequence directed against at least one splice site of at least one exon, said exon encoding a dispensable domain of dystrophin.
priorityDate 2004-08-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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