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publicationDate 2022-11-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2022241030-A1
titleOfInvention Treatment of duchenne muscular dystrophy and combinations thereof
abstract Provided are methods of treating or ameliorating the symptoms of dystrophinopathies, such as Duchenne muscular dystrophy and Becker muscular dystrophy by administration of therapeutically effective doses of recombinant adeno-associated viruses (rAAV) containing a transgene encoding a microdystrophin in combination with a second therapeutic which is effective to treat or ameliorate the symptoms of the dystrophinopathy.
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ29577
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11120
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48677
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ43117
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ12669
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11118
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48675
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07335
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP61859
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ24546
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ29594
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP16858
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP11121
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8Z6K2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA8MZH3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02594
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0CN75
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP61861
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID505394
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP31515
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100171544
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02593
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24907
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6IT78
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID380259
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID322327
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP61860
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ42806
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP31514
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP30613
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62160
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01651
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9ZKT0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62156
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ97BJ8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00565
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ71UH5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID403580
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0CE13
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62184
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ42954
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID397688
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP14618
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62162
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00567
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62201
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00566
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2FNA2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ71UH6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62203
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62202
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID474584
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP55964
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP75358
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48976
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396526
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID527488
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID7402
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1605
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HJ69
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62145
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB19
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9A6M9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4WIW2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62144
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB18
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID402874
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID282602
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62151
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP32647
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62149
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2317
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0R2M2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62154
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542316
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396823
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62152
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5265
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP06906
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ27957
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4344564
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4842
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO28542
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP70789
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ3IUT3
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3037233
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24383
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID368319
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00549
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO65595
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00548
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID11219835
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23239
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80322
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396725
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27161
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A0H3MAB5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9GRJ1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID450133
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ46078
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27166
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID52152
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27165
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3873434
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO27090
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP22513
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9XYF6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO30853
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15115
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ29536
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCE1C4Z7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2875471
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6LCY3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP34038
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCD3ZQL7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07310
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542367
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ44473
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80885
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4324384
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID12967
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HSS7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19883
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP18061
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ39752
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30148
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID534358
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6GG09
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5ULT9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4326903
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID336

Total number of triples: 773.