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publicationDate 2022-11-03-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2022232141-A1
titleOfInvention Microdystrophin gene therapy administration for treatment of dystrophinopathies
abstract Provided are methods of treating or ameliorating the symptoms of dystrophinopathies, such as Duchenne muscular dystrophy and Becker muscular dystrophy by administration of therapeutically effective doses of recombinant adeno-associated viruses (rAAV) containing a transgene encoding a microdystrophin.
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02138
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62203
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02135
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID374258
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100171544
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24907
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62202
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5265
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02126
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP30613
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62160
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02125
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ27957
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID74989
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62156
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID11219835
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02130
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419533131
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80322
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30216
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396725
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62184
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02129
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A0H3MAB5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27161
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9A6M9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP62162
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID359826
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID402874
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9GRJ1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ3IUT3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6GJF7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27166
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27165
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID465887
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO27090
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542316
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP55964
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15165
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00549
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6LCY3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID527488
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID516892
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00548
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HJ69
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5HIG1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4344564
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID12967
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB19
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15166
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4WIW2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB18
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07036
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419507500
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4842
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8CMT7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2317
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0R2M2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP9WND1
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID9541
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP22513
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP9WND0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15115
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396823
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP06906
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID105468624
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ29536
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCD3ZQL7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO65595
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419555018
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542367
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ44473
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5HRP0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15449
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4324384
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23020
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HSS7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO28542
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4735
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP70789
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ46078
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24383
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30148
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID52152
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID272636
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID368319
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9XYF6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID414396
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP52489
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO30853
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID2725057
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2875471
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13346
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID9544
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP17928
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9HFY6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23239
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0AC13
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80216
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID9541
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80885
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID409702108
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80271
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO32755
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21251
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07406
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP52480
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A9B3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID450133
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ99TG5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO34425
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07411
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80044
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3873434
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6906
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07409

Total number of triples: 1082.