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filingDate 2022-04-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2022-10-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2022221462-A1
titleOfInvention Vector constructs for delivery of nucleic acids encoding therapeutic vlcad or mcad and methods of using the same
abstract The present disclosure relates to nucleic acid (e.g., modified nucleic acid) sequences encoding very long-chain acyl-CoA dehydrogenase or the medium-chain acyl-CoA dehydrogenase, expression cassettes and delivery vectors comprising the same, and methods for delivery of the same for treating very long-chain acyl-CoA dehydrogenase deficiency or the medium-chain acyl-CoA dehydrogenase.
priorityDate 2021-04-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5HMA3
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ48TL1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8FHX4
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21293
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http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID11757
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7MVV7
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4ITL0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB1IE18
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21329
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID11276
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC1F0Q7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO33331
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9K6F0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB1AJN5
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID2725057
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ492N1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7N457
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ4A7B8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9VSC8
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID272636
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP17402
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP25987
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO14746
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8ZRJ7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21944
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ81JX0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC1FQ94
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID10359
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB7GMH4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8RDA1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ99ZP6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP15650
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ32GW8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45025160
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57123787
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8RLE0
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID7108
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID10245
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ28M21
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9KST9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1253269
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP65230
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB9LJ65
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID30819
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8626731
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7MLR4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5I2M3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP65231
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1209982
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID885636
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID61603857
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ927U9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5I2M4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP17653
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4811496
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6F0I2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP57926
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6YRB1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO50519
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5I2M8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP47280
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO96720
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9SPU7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID282602
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ60HI0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5I2M5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ3Z0V3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP71276
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9WGI6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5I2M7
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2897887
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2NIM1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9CHX5
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419521348
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID11807
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID36362
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3707550
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19466
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3KYH2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ82KI9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1486634
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID949007
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB3PM40
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO52951
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7NVK0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ67619
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID928935
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB7HFM8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1487307
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57133995
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24271467
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13157
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ71WN4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP47848
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1486904
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6G7J1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ57NR0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP06478
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF5HB62
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6Y1S0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ92N38
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3LFK4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ38WJ3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP18555
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1487533
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO06164
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ4KTA7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP75070
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ831F5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C781
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID11840
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C782
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13300
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID8627024
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I4
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57203972
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1488261
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9E6P5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID60923442
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA7NI79
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9PPP5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24528124
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO13339
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB7HY90
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57976491
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID888731
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0K1F4
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID832371
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2P902
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68563
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID403128
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9DXE6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO57203
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB8E001
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8K1H1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5UP25
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0C8I6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ64YL9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP22649
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID108709389
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ83A42
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ1HVD1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4194746
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ72XC1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ06163
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7UFR1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB8G6Y1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ94819
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9A7C6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ4L800
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID9796
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6HAV3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0K7G9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ47146
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9A8K3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6GEV6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC5CBS9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9CF72
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48064
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ94818
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1258712
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ65DU6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A5G4
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5953011
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID37
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB1KSQ8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0CK38
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5H631
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID54106
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID12721
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID22220432
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID1891767
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9QNF7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5HY32
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ95SX7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA7Z9S5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8VVL0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57208956
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ66AM8
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4369442
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0CK37
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9CHM8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB7IQY3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DV59
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB1L989

Total number of triples: 551.