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publicationDate 2022-04-07-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2022067398-A1
titleOfInvention Treatment of optic atrophy
abstract An isolated or purified antisense oligomer for modulating mRNA translation of the OPA1 gene transcript or part thereof which has a modified backbone structure and sequences with at least 75% sequence identity to the isolated or purified antisense oligomer.
priorityDate 2020-10-02-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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