http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2021165841-A1

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filingDate 2021-02-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_61ff2e06553b7155ba2a1de5980ca95d
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publicationDate 2021-08-26-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2021165841-A1
titleOfInvention Compound for the treatment of a glycogenosis
abstract The present invention relates to a compound selected from a polynucleotide coding for a glycogen debranching enzyme (GDE), a vector and a host cell comprising the polynucleotide. The present invention further relates to the use of the compound for the treatment of a glycogenosis (GSD), preferably GSDIII.
priorityDate 2020-02-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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