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filingDate 2020-12-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-06-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2021115317-A1
titleOfInvention Compositions and methods for treating leber's hereditary optic neuropathy with nadh dehydrogenase proteins
abstract Provided is a recombinant nucleic acid, comprising: a mitochondrial targeting sequence; a mitochondrial protein coding sequence, wherein said mitochondrial protein coding sequence encodes a polypeptide comprising a mitochondrial protein; and a 3'UTR nucleic acid sequence. Also provided is a pharmaceutical composition comprising the recombinant nucleic acid and a method of treating Leber's hereditary optic neuropathy (LHON) using the pharmaceutical composition.
priorityDate 2019-12-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8AB22
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9R0J8
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A363
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8A3I5
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID448056355
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID44129042
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA7KGA5
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA6URW1
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Total number of triples: 835.