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filingDate 2020-11-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2021-05-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2021097157-A1
titleOfInvention Treatment of hereditary angioedema with liver-specific gene therapy vectors
abstract Provided herein are compositions and methods for treating a Cl esterase inhibitor deficiency by normalizing levels of the Cl esterase inhibitor protein in a subject having HAE.
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Total number of triples: 888.