http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2021050991-A1

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filingDate 2020-09-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_4b5bd3823e5d92a0fac9d6f69cc91f43
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publicationDate 2021-03-18-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2021050991-A1
titleOfInvention Compositions and methods for treatment of friedreich's ataxia
abstract The present application provides compositions for treatment of Friedreich's Ataxia (FA). These include, but are not limited to, nucleic acid constructs and recombinant vectors comprising a human frataxin 5' untranslated region (5'UTR FXN) and a human frataxin (FXN) nucleotide sequence are provided herein. Also provided are methods for treatment of FA.
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priorityDate 2019-09-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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Total number of triples: 604.