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publicationDate 2020-10-01-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2020198706-A1
titleOfInvention Compositions and methods for ttr gene editing and treating attr amyloidosis comprising a corticosteroid or use thereof
abstract Compositions and methods for editing, e.g., introducing double-stranded breaks, within the TTR gene in combination with administration of a corticosteroid are provided. Compositions and methods for treating subjects having amyloidosis associated with transthyretin (ATTR), in which a guide RNA and a corticosteroid are administered, are provided.
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID124087
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19314
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID14433
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226425789
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID27306
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5R7P4
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID413969188
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419554184
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP60206
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID1869339
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04838
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID65109
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP60205
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226393686
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7427
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5311264
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP60204
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419554126
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419554006
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226406284
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID2471
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419554743
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5RAD2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68945
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3821
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID263
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8STF0
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419480347
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID42838
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID81605
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226491233
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID185460
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02599
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226409525

Total number of triples: 1937.