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filingDate 2020-02-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2020-08-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2020168135-A1
titleOfInvention Compositions and methods for treating alpha-1 antitrypsin deficiency
abstract The present invention features compositions and methods for editing deleterious mutations associated with alpha-1 anti-trypsin (A1AT) deficiency. In particular embodiments, the invention provides methods for correcting mutations in an A1AT polynucleotide using an adenosine deaminase base editor, ABE8, having unprecedented levels of efficiency.
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID95174
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226396811
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226397933
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135602211
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399305
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID92164
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID12310447
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID54216460
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226399167
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID1715220
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID95489
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID164608
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57285136
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID57455154
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226426764
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226397217
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID9475
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID1148
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226427915
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID994
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID96852
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID135415876
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID564
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226461237
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226426571
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226409512

Total number of triples: 328.