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filingDate 2020-01-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2020-08-06-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2020160486-A1
titleOfInvention Aav vector treatment methods for late infantile neuronal ceroid lipofuscinosis type 2
abstract Disclosed herein are methods for treating a primate in need of tripeptidyl peptidase 1 (TPP1), comprising (a) providing a recombinant adeno-associated virus (AAV) vector comprising a nucleic acid encoding TPP1; and (b) administering an amount of the recombinant AAV vector to the central nervous system (CNS) of the primate, wherein the TPP1 is expressed in the primate.
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