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publicationDate 2020-06-04-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2020113034-A1
titleOfInvention Aav viral vectors and uses thereof
abstract Disclosed herein are compositions comprising AAV9 viral vectors and methods of using them to treat SMA patients, e.g., Type II and Type III Spinal Muscular Atrophy (SMA) patients.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID549559
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5743
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5354618
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395485
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO35312
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID453421822
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395486
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID57934
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO14793
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP83456
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID65492
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226458111
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419534993
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8AVB2
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226400066
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5280352
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID1891767
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00564
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID56731807
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6J1J2
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07310
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID66939874
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100537633
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ05205
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID22227373
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP09605
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID23675756
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID45052093
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID102130507
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID280979
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP05547
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID6400916
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID61480213
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID60
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID856609
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http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3121
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Total number of triples: 381.