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publicationDate 2019-08-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2019152474-A1
titleOfInvention Gene therapy for limb-girdle muscular dystrophy type 2c
abstract The disclosure relates to gene therapy vectors, such as AAV vectors, comprising a polynucleotide encoding γ-sarcoglycan (SGCG) and methods of using such gene therapy vectors to treat subjects suffering from a muscular dystrophy, e.g. limb girdle dystrophy type 2C (LGMD2C).
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID447832
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ91493
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6442

Total number of triples: 318.