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publicationDate 2019-02-28-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2019040747-A1
titleOfInvention IN UTERO TRANSPLANTATION OF CELLS EXPRESSING FACTOR VIII FOR THE TREATMENT OF HEMOPHILIA
abstract The present invention provides a method of treating hemophilia A in a subject comprising injecting mesenchymal stem / stromal (MSC) cells modified to express high levels of factor VIII protein. MSCs are injected to the subject before birth. Modified MSCs can also express high levels of von Willebrand factor protein.
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19147
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396991
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID32751
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6Y1S0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID542367
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCH9A0J9
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB18
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP41323
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DB19
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID610457
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP10096
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2NEN0
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ01651
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2FNA2
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID477956
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP41693
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4204
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF6ZFC8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2PE74
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP55030
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A2R8QA47
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID282602
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCBAG55070
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCE2RVI8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9YFS9
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID25199600
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100301932
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2EEY0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ64467
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID71416
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO28542
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCNP_003371
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9ESV6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3133
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XJ10
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID566771
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID419031
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB6CKP4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59309
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3N6F0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID16590
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID422199
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP08505
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226395375
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19314
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP29272
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCF7EDI8
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID9606
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19315
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ12XM4
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID947
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID574282
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3NEV8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP29455
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID451773
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCM0RAA8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID7431
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48616
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO27090
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2157
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID78294
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP01012
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3MWN0
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226453098
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2158
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP10618
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48670
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ4R4X4
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID403502
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5311068
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA4YHA5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48674
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5XDW3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59800
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226416638
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA1RV79
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30256
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID109644000
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID569386
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID405790
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP00634
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO77762
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID58813
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID21667
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID50909322
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24946
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59906
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB1YD06
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396054
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP27726
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP13726
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID378783
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO34425
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24383
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5JHB5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID41682
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23722
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP42202
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP09124
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ865Y0
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID450133
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9V1P1
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9NR96
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID821323
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID406696
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID512431
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ95181
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4329892
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP79339
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID60
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID281876
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100522394
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID18613
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9MZA9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6L6X6
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID465887
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07750
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9MZR1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID11461
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9MZR8
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID317743
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ865W7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A9B3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID15978
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2210
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC6A312
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A9B5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04275
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID140599
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID338457
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC4KHW5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP04406
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID414396
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5H631

Total number of triples: 496.