http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2018226230-A1

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filingDate 2017-06-08-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e90650360f3dca10a43c54a001d061ad
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publicationDate 2018-12-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2018226230-A1
titleOfInvention Compounds and methods for treatment of diamond blackfan anemia
abstract The present invention relates generally to methods for treatment of ribosomal disorders and ribosomopathy, e.g. Diamond Blackfan anemia (DBA). In some embodiments, the invention relates to methods for the use of a small-molecule autophagy modulator for treatment of ribosomal disorders and ribosomopathy. The invention also relates to small molecule drug discovery and methods of screening compositions to determine their effectiveness for treatment of ribosomal disorders and ribosomopathies.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID3776387
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB2T9B1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID34412

Total number of triples: 1607.