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filingDate 2018-02-20-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2018-08-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2018152485-A1
titleOfInvention Gene therapy for treating familial hypercholesterolemia
abstract Regimens useful in reducing the frequency of apheresis in a human patient having familial hypercholesterolemia are described. The method involves administering to the human subject via a peripheral vein by infusion of a suspension of replication deficient recombinant adeno-associated virus (rAAV).
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP07406
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID5746
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN21
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DMC1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2539795
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7LZB9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP19646
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN26
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID281845
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP21948
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DMC0
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226411198
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5656924
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN25
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID414519
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP49183
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA8MUN2
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226411934
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN28
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID853
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP16309
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ806Y6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ6WN27
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3767
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226394780
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226402238
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02138
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9YQR5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID66939874
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02135
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DTU8
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP80044
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID46221
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02143
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP68292
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DTU7
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID10407
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DTV0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP02140
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4018
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID445643
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID395103
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID30216
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP24292
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO97398
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0A1S3EL69
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0DTU9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP35002
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID49787044

Total number of triples: 693.