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publicationDate 2018-04-19-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2018071216-A1
titleOfInvention Methods and compositions for treating genetic eye diseases
abstract The present disclosure provides CAPN5 substrates and CAPN5 inhibitors, nucleic acids encoding CAPN5 substrates or CAPN5 inhibitors, methods to deliver CAPN5 substrate or CAPN5 inhibitor agents to the eye, and methods of identifying inhibitors of CAPN5.
priorityDate 2016-10-11-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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