Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_b1e472e52510b9a0150fb8bb983e5c5a |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-33 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3145 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3233 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-712 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K31-7125 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P21-00 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61P25-14 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K31-7088 http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/C12N15-11 |
filingDate |
2016-08-26-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_e71c3b9b7ce1c2b2c8aefd550bfa66e1 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_896539bbc0e3d1e0b591010f31e32cad |
publicationDate |
2017-03-09-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
WO-2017040271-A1 |
titleOfInvention |
Modified antisense oligomers for exon inclusion in spinal muscular atrophy |
abstract |
The present disclosure relates to modified antisense oligomers and related compositions and methods for increasing the expression of functional SMN protein and methods for treating spinal muscular atrophy and relates to inducing inclusion of exon 7 in SMN2 mRNA. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11555189-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3697910-A4 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11299737-B1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/JP-2021500016-A |
priorityDate |
2015-08-28-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |