http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2016210170-A9

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filingDate 2016-06-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_9e9cf1d8e7a3af981b07a9df7cb241f7
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publicationDate 2018-02-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2016210170-A9
titleOfInvention Modified factor ix, and compositions, methods and uses for gene transfer to cells, organs and tissues
abstract The invention relates to modified Factor IX coding sequence, expression cassette, vectors such as viral (e.g., lenti- or adeno-associated viral) vectors, and gene transfer methods and uses.In particular, to target Factor IX nucleic acid to cells, tissues or organs for expression (transcription) of Factor IX.
priorityDate 2015-06-23-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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