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publicationDate 2015-12-30-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2015197869-A1
titleOfInvention Efficient systemic treatment of dystrophic pathologies
abstract A composition comprising a gene therapy product for use in the treatment of a dystrophic disease in a subject, advantageously in humans, wherein: the gene therapy product comprises a nucleic acid sequence encoding a functional microdystrophin; the composition is systemically administered.
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID845221
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ94819
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID449517
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID450133
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ25BC1
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID806979
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID537655
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID396991
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID506155
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9XSJ6
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID426132189
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4271646
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4961700
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID23305
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO70372
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP23239
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4783267
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID117243
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5R9U1
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4099902
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4964866
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID2896181
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID13138
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID574282
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID803150
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4266807
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http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP48675
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6443
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8SQ72
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID1461021
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http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID24373
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Total number of triples: 449.