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publicationDate 2015-09-17-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2015138348-A1
titleOfInvention Compositions useful in treatment of ornithine transcarbamylase (otc) deficiency
abstract Viral vectors comprising engineered hOTC DNA and RNA sequences are provided which when delivered to a subject in need thereof are useful for treating hyperammonemia, ornithine transcarbamylase transcarbamylase deficiency and symptoms associated therewith. Also provided are methods of using hOTC for treatment of liver fibrosis cirrhosis in OTCD patients by administering hOTC.
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http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID128126417
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID853
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ9KPQ0
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ1K8F6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ59MB6
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ8R4H7
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID23615254
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA3N062
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ06163
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID569750
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ95SX7
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ1KVQ9
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID999
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID3724
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID9571131
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB5FAS8
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419565992
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ0CY06
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID128983203
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID25377
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5DA88
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID129598381
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID564060
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB0CR45
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419584632
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA9MS91
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID361042
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA7TQL5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ2UES9
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA5DWN5
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID282856
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID453652
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID395735
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419514679
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5106
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID856103
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID7058172
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID4947
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCO00939
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID885462
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID11699
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ65UJ9
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID6906
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226443942
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID19161
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID449559927
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ7N8S4
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP22567
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID280887
http://rdf.ncbi.nlm.nih.gov/pubchem/taxonomy/TAXID9593
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCA0KLC8
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID226396167
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID33274
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ1DNE1
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB6H6F3
http://rdf.ncbi.nlm.nih.gov/pubchem/anatomy/ANATOMYID35269
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID32199
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ5B0R3
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCC3K3V3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID4046
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCB9W7S3
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID5009
http://rdf.ncbi.nlm.nih.gov/pubchem/compound/CID15047
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419563898
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID54281
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ1PS67
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID47220
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCE7FCP8
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID419522837
http://rdf.ncbi.nlm.nih.gov/pubchem/gene/GID100536902
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A6C5
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCQ06SH2
http://rdf.ncbi.nlm.nih.gov/pubchem/protein/ACCP0A6C6
http://rdf.ncbi.nlm.nih.gov/pubchem/substance/SID451761003

Total number of triples: 377.