http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2015009596-A2

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assignee http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_487a9e3f4bf6aedc597e3497b7c981ab
classificationCPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/A61K45-06
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12Y302-0102
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classificationIPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K38-47
filingDate 2014-07-14-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_f024dfd6ca6f46c9d052cfcef48884ba
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_aa0ab09eecfedf435fd25d63c391d81c
publicationDate 2015-01-22-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2015009596-A2
titleOfInvention Methods and oral formulations for enzyme replacement therapy of human lysosomal and metabolic diseases
abstract The invention provides methods, compositions and kits for enzyme replacement therapy as well as molecular constructs, cells, tissues and plants suitable for expressing recombinant enzymes. Similarly, the invention provides methods for recombinantly producing and orally administering certain metabolic or lysosomal enzymes such as acid alpha glucosidase (GAA) alone, in a pharmaceutical composition or with an activator protein (AGA). Also, the invention provides methods for treating a glycogen storage disease type Π (GSDII) or acid maltase deficiency (AMD) or Pompe disease or Fabry disease.
priorityDate 2013-07-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
type http://data.epo.org/linked-data/def/patent/Publication

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Total number of triples: 602.