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publicationNumber WO-2014124282-A1
titleOfInvention Enhanced aav-mediated gene transfer for retinal therapies
abstract Described herein are capsid proteins and adeno-associated viruses capable of targeting various types of ocular cells including bipolar and horizontal cells. Also described herein are methods of treating various ocular disorders in a subject in need thereof by administering to the subject an effective concentration of a composition comprising the recombinant adeno-associated virus (AAV) of the invention.
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Total number of triples: 880.