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filingDate 2013-11-29-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_36373cdf4403c9ba180e3b7e38f77c79
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publicationDate 2014-06-12-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2014086687-A1
titleOfInvention A cftr corrector for the teatment of genetic disorders affecting striated muscle
abstract The present invention relates to the use of CFTR correctors in the treatment of genetic disorders affecting striated muscle selected from sarcoglycanopathies, Brody's disease (BD) and the recessive forms of Cathecolaminergic Polymorphic Ventricular Tachycardia (CPVT).
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Total number of triples: 388.