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inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_255949118506d2b556616fc311a8dc71
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publicationDate 2014-02-13-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2014025887-A1
titleOfInvention Selective reactivation of genes on the inactive x chromosome
abstract Methods and compositions for selectively reactivating genes on the inactive X chromosome (Xi) in a locus-specific manner, e.g., genes associated with X-linked diseases, e.g., Rett Syndrome, Factor VIII or IX deficiency, Fragile X Syndrome, Duchenne muscular dystrophy, and PNH, in heterozygous females.
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