Predicate |
Object |
assignee |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_df61f302b68cd4f1f275b00300d1226a http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_29a85b86d4e0ab74f93fce88f8749928 http://rdf.ncbi.nlm.nih.gov/pubchem/patentassignee/MD5_b3c2e77f8dfda692ca527454d23ecc03 |
classificationCPCAdditional |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-314 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-11 http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N2310-3233 |
classificationCPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentcpc/C12N15-113 |
classificationIPCInventive |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00 |
filingDate |
2013-02-09-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
inventor |
http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8635ceb44b2eacf4c088da42c0a4e2c1 http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_28b6c2b1573095b36c19ff433d6ac252 |
publicationDate |
2013-08-15-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
publicationNumber |
WO-2013120038-A2 |
titleOfInvention |
Morpholino targeting dux4 for treating fshd |
abstract |
A composition and method is provided that comprises a morpholino oligonucleotide capable of inhibiting DUX4 expression. The morpholino oligonucleotide can provide a therapeutic effect in individuals with facioscapulohumeral muscular dystrophy. Further, the composition and method may comprise a dendrimer delivery moiety. |
isCitedBy |
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10258628-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10538763-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/EP-3420109-A4 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11180755-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-11345913-B2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2017050836-A1 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/RU-2768289-C2 http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2016195493-A1 |
priorityDate |
2012-02-10-04:00^^<http://www.w3.org/2001/XMLSchema#date> |
type |
http://data.epo.org/linked-data/def/patent/Publication |