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classificationIPCInventive http://rdf.ncbi.nlm.nih.gov/pubchem/patentipc/A61K48-00
filingDate 2013-02-09-04:00^^<http://www.w3.org/2001/XMLSchema#date>
inventor http://rdf.ncbi.nlm.nih.gov/pubchem/patentinventor/MD5_8635ceb44b2eacf4c088da42c0a4e2c1
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publicationDate 2013-08-15-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2013120038-A2
titleOfInvention Morpholino targeting dux4 for treating fshd
abstract A composition and method is provided that comprises a morpholino oligonucleotide capable of inhibiting DUX4 expression. The morpholino oligonucleotide can provide a therapeutic effect in individuals with facioscapulohumeral muscular dystrophy. Further, the composition and method may comprise a dendrimer delivery moiety.
isCitedBy http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10258628-B2
http://rdf.ncbi.nlm.nih.gov/pubchem/patent/US-10538763-B2
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http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2017050836-A1
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http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2016195493-A1
priorityDate 2012-02-10-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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