http://rdf.ncbi.nlm.nih.gov/pubchem/patent/WO-2013016595-A1

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filingDate 2012-07-27-04:00^^<http://www.w3.org/2001/XMLSchema#date>
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publicationDate 2013-01-31-04:00^^<http://www.w3.org/2001/XMLSchema#date>
publicationNumber WO-2013016595-A1
titleOfInvention Exonic splicing enhancers and exonic splicing silencers
abstract Compounds and methods for regulation of exonic splicing enhancers and exonic splicing silencers. Compounds include polynucleotides targeted to aberrant exonic splicing enhancers and exonic splicing silencers. Compounds and methods for the diagnosis of diseases and conditions associated with aberrant exonic splicing enhancers and exonic splicing silencers. Methods for identifying splicing-sensitive disease mutations, and functional RNA elements as targets for amelioration of aberrant pre-mRNA splicing.
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